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## The Leader in RNAi Therapeutics Medicines based on RNAi work by “silencing” or disabling the production (“expression”) of the genes that cause specific diseases. Since our medicines work at a genetic level, we believe that we can develop small interfering RNAs that can silence virtually any gene in the genome, meani
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Frontline care navigators and community health workers help patients navigate health systems and access essential services, including preventive screenings, food, housing, and transportation.
AlnylamChallengershealthfrontlinecarenavigatorscommunityworkers
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## How Our RNAi Therapeutics are Made siRNA (small interfering RNA) manufacturing provides the chemical building blocks that form the drug substance of our RNAi therapeutics and other genetically-based therapeutic technologies. This type of manufacturing is a complex, time-consuming process that requires specialized fa
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## PH1 Manifestations Can Vary By Stage of Life Patients can be diagnosed with PH1 at any age, but most individuals experience their first symptoms in early childhood. Below are some examples of possible symptoms, but are not limited to such.
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## Additional Alnylam Resources We are committed to supporting patients and their families throughout their journey with a wide range of programs and services—from diagnosis to access to treatment and care.
PatientAdvocacyadditionalalnylamresourcescommittedsupportingpatients
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## Alnylam Is Employee-Driven “Change the world” kind of people tend to have a lot of good ideas, and a lot of passion for those good ideas. We love that and empower our employees to bring those ideas to life, within both Alnylam and our communities, through Employee Resource Networks (ERNs) or other types of employee-
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## Transformando o Tratamento de Doenças Nossas terapias inovadoras de RNAi silenciam genes que causam ou contribuem para doenças
Portugudoentransformandotratamentonossasterapiasinovadorasrnai
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## Silence Disease. Amplify Life. When RNAi silences the genes that cause disease, the best parts of life can be amplified.
Dansksilencediseaseamplifylifernaisilencesgenes
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## Silence Disease. Amplify Life. When RNAi silences the genes that cause disease, the best parts of life can be amplified.
Svenskasilencediseaseamplifylifernaisilencesgenes
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